We the Scientists How a Daring Team of Parents and Doctors Forged a New Path for Medicine [Audiobook] [#544310]

We the Scientists: How a Daring Team of Parents and Doctors Forged a New Path for Medicine (Audiobook)
English | ASIN: B0B6244SK5 | 2023 | 4 hours and 49 minutes | M4B@128 kbps | 268 MB
Author: Amy Dockser Marcus
Narrator: Kristen DiMercurio
A Pulitzer Prize-winning reporter's moving narrative of a group of patient advocates who are revolutionizing the way medical research is conducted. For more than half a century, medical advances have been driven by investigators launching experiments inside labs. Science is often conducted in isolation and geared toward the long view. This is the story of a group of people who tried to force the lab doors open: parents whose children had been diagnosed with a rare and fatal genetic condition known as Niemann-Pick disease type C. The disease prevents cells from processing cholesterol, which leads to the progressive loss of the brain's and the body's ability to function. Recognizing that there would never be a treatment in time to save their children if things stayed the same, the parents set up a collaboration with researchers and doctors in search of a cure.